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Arthex Biotech
Drug discovery of anti-microRNAs
involved in neuromuscular disease.
Discover our investigational compounds
Antisense oligonucleotide against a miRNA (antimiR)
New Target
miRNA Upregulated in patient muscles
First in class Mechanism of Action
Impact on the roots of the disease (DMPK gene and MBNL proteins)
Improve muscle
Delivery
Oligonucleotide conjugated to a fatty acid: very low effective dose