Arthex Biotech

Drug discovery of anti-microRNAs
involved in neuromuscular disease.

Discover our investigational compounds

Antisense oligonucleotide against a miRNA (antimiR)

New Target
miRNA Upregulated in patient muscles
First in class Mechanism of Action
Impact on the roots of the disease (DMPK gene and MBNL proteins)
Improve muscle
Oligonucleotide conjugated to a fatty acid: very low effective dose